Klotho is advancing its ALS gene therapy candidate KLTO‑202 to the manufacturing phase, and is planning the first human ...

The FDA granted orphan drug designation to Sineugene Therapeutics' SNUG01, a first-in-class experimental gene therapy for ...

As her husband's ALS journey extends, columnist Kristin Neva considers finally "settling in," so to speak, by securing a better bed.

Clene is continuing to work with U.S. regulators on its plans to seek accelerated approval of CNM-Au8 for the treatment of ...

A Q&A with author and activist Mindy Uhrlaub, who shares how she is using her voice to raise awareness and support for the ...