The drug, Dawnzera, is approved to prevent symptoms of a rare genetic disease called hereditary angioedema (HAE) in adults and pediatric patients over 12 years old. The condition causes frequent ...

A little boy in the Chicago area is battling a rare disease and desperately needs a drug treatment for a better life. The ...

Ionis Pharmaceuticals won FDA approval for a drug that prevents painful swelling attacks triggered by a rare genetic condition, hereditary angioedema.

Dawnzera is the third medicine cleared by U.S. regulators this year for the rare genetic condition, and the second wholly owned medicine Ionis has brought to market.

Rhythm Pharmaceuticals (NASDAQ:RYTM) announced that U.S. and EU regulators have accepted for review a potential label ...

Attorney General Kris Mayes wants the U.S. Food and Drug Administration to remove restrictions on one of two drugs used in non-surgical abortions.

An herbal supplement that’s marketed as a cure-all for chronic pain and sold in gas stations and smoke shops is getting ...

Krystal Biotech, Inc. (the 'Company”) (NASDAQ: KRYS), a commercial-stage biotechnology company, today announced an update on development plans for KB707, the Company’s redosable immunotherapy designed ...

Women using Ozempic and similar drugs are reporting changes in the vulva area, termed 'Ozempic vulva,' including sagging, ...

In 2024, Hurricane Helene triggered a nationwide shortage of the country's intravenous (IV) fluids after damaging a facility in North Carolina. A similar IV fluid shortage was caused when Hurricane ...

Feeding rats edible microbeads designed to absorb fat helps them lose weight. One day the beads could be used in human foods and drinks to prevent or treat obesity in people.

The FDA has agreed to speed up a review of a rare disease drug developed by Stealth BioTherapeutics, a notable step after the company said it may have to close its doors otherwise.